SmileLines

Foundation news, research updates and more.

07 Nov

BIG NEWS: Prosensa Exon Skipping Therapy Closing In!

Posted in Research updates, Two Smiles News on 07.11.09 by Merlyn

It was announced this week that human clinical trials of the exon skipping drug PRO051 will begin early next Spring in a collaborative effort between Prosensa and GlaxoSmithKline.  The trials will take place in Columbus, Ohio starting in March, 2010 and will involve direct injection therapy as well as intravenous therapy in a double blind placebo format to further the efficacy and dosing parameters for the compound as well as broaden research data on recipients of the drug.  Contact with a researcher involved in establishing the trial has been made and it is our every intention to involve Nolan and Jack in the trial if at all possible.  This therapy has long been thought to be extremely viable and has proven reliable in both computer, animal, and preliminary human trials.  Please follow the link below to the press release which highlights this development and keep hoping for this miracle to come true!

http://prosensa.eu/news/Press%20Release%20GSK%20-%20Prosensa.pdf

Continued smiles,

Matt

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